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Organic Acidemia

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Physiology, Microbiome and Biochemistry Studies of Propionic

Recruiting
  • Metabolic Disease
  • +2 more
    • Bethesda, Maryland
    • +1 more
    Aug 17, 2022

    Organic Acidemia, Cognitive Orientation Trial in Ankara (The Cognitive Orientation to Daily Occupational Performance (CO-OP)

    Completed
    • Organic Acidemia
    • Cognitive Orientation
    • The Cognitive Orientation to Daily Occupational Performance (CO-OP) Approach
    • Home Program
    • Ankara, Altindag, Turkey
      Hacettepe University
    Oct 13, 2021

    Healthy Volunteers, Propionic Acidemia, Methylmalonic Acidemia Trial in Topeka, Pittsburgh, Austin (BBP-671, Placebo)

    Recruiting
    • Healthy Volunteers
    • +3 more
    • Topeka, Indiana
    • +2 more
    Apr 8, 2022

    Systemic Biomarkers of Brain Injury From Hyperammonemia

    Recruiting
    • Urea Cycle Disorder
    • +5 more
      • Washington, District of Columbia
        Children's National Research Institute
      Oct 25, 2021

      Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) Trial in Taipei (Carglumic Acid (Carbaglu®))

      Unknown status
      • Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA)
      • Carglumic Acid (Carbaglu®)
      • Taipei, Taiwan
        National Taiwan University Hospital
      Feb 25, 2020

      "The MaP Study": Mapping the Patient Journey in MMA and PA

      Completed
      • Methylmalonic Acidemia
      • Propionic Acidemia
        • Stanford, California
        • +16 more
        Jul 29, 2021

        Organic Acidemia CARBAGLU®: A Mixed Methods Approach

        Unknown status
        • Methylmalonic Acidemia
        • Propionic Acidemia
        • Carglumic Acid
        • Bordeaux, France
        • +20 more
        Jan 8, 2020

        Methylmalonic Acidemia, Propionic Acidemia Trial in San Francisco, Remote (Registry)

        Recruiting
        • Methylmalonic Acidemia
        • Propionic Acidemia
        • Registry
        • San Francisco, California
        • +2 more
        Jun 27, 2022

        Methylmalonic Acidemia, Propionic Acidemia Trial in United States (HST5040, Placebo)

        Recruiting
        • Methylmalonic Acidemia
        • Propionic Acidemia
        • San Diego, California
        • +10 more
        Sep 6, 2022

        Methylmalonic Acidemia Trial in United States (hLB-001)

        Recruiting
        • Methylmalonic Acidemia
        • hLB-001
        • Atlanta, Georgia
        • +3 more
        Aug 16, 2022

        A Non-Interventional Post-Authorization Study of Carbaglu for

        Enrolling by invitation
        • Hyperammonemia
        • +2 more
        • carglumic acid
        • Indianapolis, Indiana
          Riley Children's Hospital
        Apr 24, 2023

        Incidence of Metabolic Disorders in Neonatal Convulsions

        Not yet recruiting
        • Neonatal Convulsions
        • MRI
        • (no location specified)
        Nov 6, 2023

        Propionic Acidemia Trial in Canada, United Kingdom, United States (mRNA-3927)

        Recruiting
        • Propionic Acidemia
        • mRNA-3927
        • Ann Arbor, Michigan
        • +4 more
        Mar 14, 2022

        Methylmalonic Acidemia (MMA) Trial run by the Selecta Biosciences, Inc. (SEL-302)

        Recruiting
        • Methylmalonic Acidemia (MMA)
        • Bethesda, Maryland
          National Human Genome Research Institute, National Institutes of
        Mar 9, 2023

        Propionic/Methylmalonic Acidemias, Maple Syrup Urine Disease, Citrullinemia Trial in Aktobe (Obtaining Dry Blood Spots From

        Recruiting
        • Propionic/Methylmalonic Acidemias
        • +28 more
        • Obtaining Dry Blood Spots From Healthy Newborns (Aged 1-7 Days)
        • +5 more
        • Aktobe, Aktobe Region, Kazakhstan
          Regional perinatal center of Aktobe region
        Jun 8, 2023

        Characterize Participants With Propionic Acidemia

        Not yet recruiting
        • Propionic Acidemia
          • (no location specified)
          Mar 3, 2023

          Fetal Acidemia Trial in Beijing (Optiflow high-flow nasal cannula system)

          Not yet recruiting
          • Fetal Acidemia
          • Optiflow high-flow nasal cannula system
          • Beijing, Beijing, China
            Beijing tongren Hospital, Capital Medical University
          Jun 25, 2023

          Methylmalonic Acidemia Trial in Birmingham (mRNA-3705)

          Recruiting
          • Methylmalonic Acidemia
          • Toronto, Ontario, Canada
          • +1 more
          Dec 20, 2022

          Metabolic Acidosis, Acute Kidney Injury Trial in Montpellier (Sodium bicarbonate infusion)

          Recruiting
          • Metabolic Acidosis
          • Acute Kidney Injury
          • Sodium bicarbonate infusion
          • Montpellier, France
            Service de médecine intensive et réanimation
          Feb 11, 2022

          Stress, Infertility, Female Trial (Organic Conceptions mindset management program)

          Not yet recruiting
          • Stress
          • Infertility, Female
          • Organic Conceptions mindset management program
          • (no location specified)
          Aug 9, 2023

          Breath Metabolomics in the Laboring Parturient

          Suspended
          • Labor Onset and Length Abnormalities
          • Breath Sample
          • Stanford, California
            Lucile Packard Children Hospital
          Oct 18, 2022

          FIT and Fecal Calprotectin in Chronic Lower GI Symptoms

          Enrolling by invitation
          • Colorectal Cancer
          • +2 more
          • Fecal calprotectin
          • Fecal immunochemical test
          • Bangkok, Thailand
            Gastroenterology division, Faculty of Medicine, Siriraj Hospital
          Aug 22, 2022

          Smoking Behaviors Trial in Reno, Philadelphia (Cigarette trial)

          Recruiting
          • Smoking Behaviors
          • Cigarette trial
          • Reno, Nevada
          • +2 more
          Jul 18, 2022

          Female Infertility Trial in Brest, Nantes, Rennes (Self-administered questionnaire and blood and urine samples)

          Completed
          • Female Infertility
          • Self-administered questionnaire and blood and urine samples
          • Brest, France
          • +4 more
          Jan 10, 2023

          Organic Compounds and Postoperative Delirum

          Not yet recruiting
          • Identify Postoperative Delirium Using Exhaled Gas Patterns
          • No intervention
          • (no location specified)
          May 15, 2023